408. Safety of Lysosomal Enzymes Over-Expression in HSC for Gene Therapy of Storage Disorders
Biffi, Alessandra, Visigalli, Ilaria, Cesani, Martina, Capotondo, Alessia, Santoni de Sio, Francesca R., Pallavicini, Isabella, Zingale, Anna, Naldini, LuigiVolume:
13
Language:
english
Journal:
Molecular Therapy
DOI:
10.1016/j.ymthe.2006.08.471
Date:
May, 2006
File:
PDF, 82 KB
english, 2006