404. Therapeutic Correction of PKU in a Mouse Model by Ectopic Expression of PAH and Its BH4- Cofactor Genes in Skeletal Muscle by a Recombinant Triple-Cistronic AAV2-Based Pseudotype 1 Vector
Ding, Zhaobing, O. Harding, Cary, Rebuffat, Alexandre, Elzaouk, Lina, Wolff, Jon A., Thony, BeatVolume:
13
Language:
english
Journal:
Molecular Therapy
DOI:
10.1016/j.ymthe.2006.08.467
Date:
May, 2006
File:
PDF, 95 KB
english, 2006