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908. Design and Optimization of U7snRNAs for Skipping of Exon 51 in DMD: Promising Tools for Future Clinical Trials
Goyenvalle, Aurelie, Vulin, Adeline, Lorain, Stephanie, Aartsma-Rus, Annemieke, van Deutekom, Judith C.T., Danos, Olivier, Garcia, LuisVolume:
13
Language:
english
Journal:
Molecular Therapy
DOI:
10.1016/j.ymthe.2006.08.998
Date:
May, 2006
File:
PDF, 90 KB
english, 2006