341. Lentiviral Vector-Mediated Gene Therapy as Treatment for Wiskott-Aldrich Syndrome (WAS): Pre-Clinical Studies in Human Cell Lines and WASp -/- Mice
HUMBLETBARON, S, ANOVER, S, KIPP, K, ZHU, Q, YE, P, ZHANG, W, OVECHKINA, Y, KHIM, S, ASTRAKHAN, A, STROM, TVolume:
11
Language:
english
Journal:
Molecular Therapy
DOI:
10.1016/j.ymthe.2005.06.344
Date:
August, 2005
File:
PDF, 79 KB
english, 2005