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563. Correction of Glycogen Storage Disease Type II by Systemic Delivery of an AAV2/8 Vector Containing a Muscle-Specific Promoter
Sun, Baodong, Li, Ping, Talmage, Brown, Andrew, Bird, Yan, Zhen, Koeberl, Dwight D.Volume:
13
Language:
english
Journal:
Molecular Therapy
DOI:
10.1016/j.ymthe.2006.08.636
Date:
May, 2006
File:
PDF, 89 KB
english, 2006