Long-term Exon Skipping Studies With 2′-O-Methyl Phosphorothioate Antisense Oligonucleotides in Dystrophic Mouse Models
Tanganyika-de Winter, Christa L, Heemskerk, Hans, Karnaoukh, Tatyana G, van Putten, Maaike, de Kimpe, Sjef J, van Deutekom, Judith, Aartsma-Rus, AnnemiekeVolume:
1
Language:
english
Journal:
Molecular Therapy — Nucleic Acids
DOI:
10.1038/mtna.2012.38
Date:
September, 2012
File:
PDF, 1.70 MB
english, 2012