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Antisense Oligonucleotide (AON)-based Therapy for Leber Congenital Amaurosis Caused by a Frequent Mutation in CEP290
Collin, Rob WJ, den Hollander, Anneke I, van der Velde-Visser, Saskia D, Bennicelli, Jeannette, Bennett, Jean, Cremers, Frans PMVolume:
1
Language:
english
Journal:
Molecular Therapy — Nucleic Acids
DOI:
10.1038/mtna.2012.3
Date:
March, 2012
File:
PDF, 589 KB
english, 2012