Exon skipping restores dystrophin expression, but fails to prevent disease progression in later stage dystrophic dko mice
Wu, B, Cloer, C, Lu, P, Milazi, S, Shaban, M, Shah, S N, Marston-Poe, L, Moulton, H M, Lu, Q LVolume:
21
Language:
english
Journal:
Gene Therapy
DOI:
10.1038/gt.2014.53
Date:
September, 2014
File:
PDF, 3.55 MB
english, 2014