Lentiviral Gene Therapy Using Cellular Promoters Cures Type 1 Gaucher Disease in Mice
Dahl, Maria, Doyle, Alexander, Olsson, Karin, Månsson, Jan-Eric, Marques, André R A, Mirzaian, Mina, Aerts, Johannes M, Ehinger, Mats, Rothe, Michael, Modlich, Ute, Schambach, Axel, Karlsson, StefanVolume:
23
Language:
english
Journal:
Molecular Therapy
DOI:
10.1038/mt.2015.16
Date:
May, 2015
File:
PDF, 2.52 MB
english, 2015