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Novel recombinant human acid α-glucosidase with optimal glycosylation is significantly better than standard of care enzyme replacement for glycogen clearance in skeletal muscles of GAA knock-out mice
Gotschall, Russell, Xu, Su, Lun, Yi, Schilling, Adriane, Soska, Rebecca, Frascella, Michelle, Garcia, Anadina, Feng, Jessie, Chang, Kate, Brignol, Nastry, Khanna, Richie, Valenzano, Kenneth J., Do, HuVolume:
114
Language:
english
Journal:
Molecular Genetics and Metabolism
DOI:
10.1016/j.ymgme.2014.12.096
Date:
February, 2015
File:
PDF, 54 KB
english, 2015