Clinical characterisation of Becker muscular dystrophy patients predicts favourable outcome in exon-skipping therapy
van den Bergen, J. C., Schade van Westrum, S. M., Dekker, L., van der Kooi, A. J., de Visser, M., Wokke, B. H. A., Straathof, C. S., Hulsker, M. A., Aartsma-Rus, A., Verschuuren, J. J., Ginjaar, H. B.Volume:
85
Language:
english
Journal:
Journal of Neurology, Neurosurgery & Psychiatry
DOI:
10.1136/jnnp-2012-304729
Date:
January, 2014
File:
PDF, 591 KB
english, 2014