Ameliorating pathogenesis by removing an exon containing a missense mutation: a potential exon-skipping therapy for laminopathies
Scharner, J, Figeac, N, Ellis, J A, Zammit, P SVolume:
22
Language:
english
Journal:
Gene Therapy
DOI:
10.1038/gt.2015.8
Date:
June, 2015
File:
PDF, 5.33 MB
english, 2015