Correction of Dystrophin Expression in Cells From Duchenne Muscular Dystrophy Patients Through Genomic Excision of Exon 51 by Zinc Finger Nucleases
Ousterout, David G, Kabadi, Ami M, Thakore, Pratiksha I, Perez-Pinera, Pablo, Brown, Matthew T, Majoros, William H, Reddy, Timothy E, Gersbach, Charles AVolume:
23
Language:
english
Journal:
Molecular Therapy
DOI:
10.1038/mt.2014.234
Date:
March, 2015
File:
PDF, 1.15 MB
english, 2015