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Transfer of genetic therapy across human populations: molecular targets for increasing patient coverage in repeat expansion diseases
Varela, Miguel A, Curtis, Helen J, Douglas, Andrew GL, Hammond, Suzan M, O'Loughlin, Aisling J, Sobrido, Maria J, Scholefield, Janine, Wood, Matthew JALanguage:
english
Journal:
European Journal of Human Genetics
DOI:
10.1038/ejhg.2015.94
Date:
May, 2015
File:
PDF, 686 KB
english, 2015