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In vivo genome editing using nuclease-encoding mRNA corrects SP-B deficiency
Mahiny, Azita J, Dewerth, Alexander, Mays, Lauren E, Alkhaled, Mohammed, Mothes, Benedikt, Malaeksefat, Emad, Loretz, Brigitta, Rottenberger, Jennifer, Brosch, Darina M, Reautschnig, Philipp, SurapolcLanguage:
english
Journal:
Nature Biotechnology
DOI:
10.1038/nbt.3241
Date:
May, 2015
File:
PDF, 1.13 MB
english, 2015