In Vitro Evaluation of a Novel mRNA-Based Therapeutic Strategy for the Treatment of Patients Suffering from Alpha-1-Antitrypsin Deficiency
Michel, Tatjana, Kankura, Anna, Salinas Medina, Martha L., Kurz, Julia, Behring, Andreas, Avci-Adali, Meltem, Nolte, Andrea, Schlensak, Christian, Wendel, Hans Peter, Krajewski, StefanieLanguage:
english
Journal:
Nucleic Acid Therapeutics
DOI:
10.1089/nat.2015.0537
Date:
June, 2015
File:
PDF, 487 KB
english, 2015