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Early treatment with laronidase improves clinical outcomes in patients with attenuated MPS I: Analysis of eight sibling pairs
Pleat, Rebecca, Al-Sannaa, Nouriya, Barbouth, Deborah S., Benhayoun, Youssef, Goizet, Cyril, Guelbert, Norberto, Jones, Simon A., Kyosen, Sandra, Martins, Ana Maria, Phornphutkul, Chanika, Reig, CeliaVolume:
114
Language:
english
Journal:
Molecular Genetics and Metabolism
DOI:
10.1016/j.ymgme.2014.12.208
Date:
February, 2015
File:
PDF, 84 KB
english, 2015