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Long-term safety and efficacy of sapropterin: The PKUDOS registry experience
Longo, Nicola, Arnold, Georgianne L., Pridjian, Gabriella, Enns, Gregory M., Ficicioglu, Can, Parker, Susan, Cohen-Pfeffer, Jessica L.Volume:
114
Language:
english
Journal:
Molecular Genetics and Metabolism
DOI:
10.1016/j.ymgme.2015.02.003
Date:
April, 2015
File:
PDF, 436 KB
english, 2015