Cellular trafficking determines the exon skipping activity of Pip6a-PMO in mdx skeletal and cardiac muscle cells
Lehto, T., Castillo Alvarez, A., Gauck, S., Gait, M. J., Coursindel, T., Wood, M. J. A., Lebleu, B., Boisguerin, P.Volume:
42
Language:
english
Journal:
Nucleic Acids Research
DOI:
10.1093/nar/gkt1220
Date:
March, 2014
File:
PDF, 7.74 MB
english, 2014