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Therapeutic Response in Feline Sandhoff Disease Despite Immunity to Intracranial Gene Therapy
Bradbury, Allison M, Cochran, J Nicholas, McCurdy, Victoria J, Johnson, Aime K, Brunson, Brandon L, Gray-Edwards, Heather, Leroy, Stanley G, Hwang, Misako, Randle, Ashley N, Jackson, Laura S, MorrisonVolume:
21
Language:
english
Journal:
Molecular Therapy
DOI:
10.1038/mt.2013.86
Date:
July, 2013
File:
PDF, 915 KB
english, 2013