AAV6-mediated Systemic shRNA Delivery Reverses Disease in a Mouse Model of Facioscapulohumeral Muscular Dystrophy
Bortolanza, Sergia, Nonis, Alessandro, Sanvito, Francesca, Maciotta, Simona, Sitia, Giovanni, Wei, Jessica, Torrente, Yvan, Di Serio, Clelia, Chamberlain, Joel R, Gabellini, DavideVolume:
19
Language:
english
Journal:
Molecular Therapy
DOI:
10.1038/mt.2011.153
Date:
November, 2011
File:
PDF, 908 KB
english, 2011