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MicroRNA-regulated, Systemically Delivered rAAV9: A Step Closer to CNS-restricted Transgene Expression
Xie, Jun, Xie, Qing, Zhang, Hongwei, Ameres, Stefan L, Hung, Jui-Hung, Su, Qin, He, Ran, Mu, Xin, Seher Ahmed, Seemin, Park, Soyeon, Kato, Hiroki, Li, Chengjian, Mueller, Christian, Mello, Craig C, WeVolume:
19
Language:
english
Journal:
Molecular Therapy
DOI:
10.1038/mt.2010.279
Date:
March, 2011
File:
PDF, 890 KB
english, 2011