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Restoration of SMN Function: Delivery of a Trans-splicing RNA Re-directs SMN2 Pre-mRNA Splicing
Coady, Tristan H, Shababi, Monir, Tullis, Gregory E, Lorson, Christian LVolume:
15
Language:
english
Journal:
Molecular Therapy
DOI:
10.1038/sj.mt.6300222
Date:
August, 2007
File:
PDF, 334 KB
english, 2007