Sustained Enzymatic Correction by rAAV-Mediated Liver Gene Therapy Protects Against Induced Motor Neuropathy in Acute Porphyria Mice
Unzu, Carmen, Sampedro, Ana, Mauleón, Itsaso, Alegre, Manuel, Beattie, Stuart G, de Salamanca, Rafael Enríquez, Snapper, Jolanda, Twisk, Jaap, Petry, Harald, González-Aseguinolaza, Gloria, Artieda, JuVolume:
19
Language:
english
Journal:
Molecular Therapy
DOI:
10.1038/mt.2010.210
Date:
February, 2011
File:
PDF, 288 KB
english, 2011