Enzyme Replacement Improves Ataxic Gait and Central Nervous System Histopathology in a Mouse Model of Metachromatic Leukodystrophy
Matzner, Ulrich, Lüllmann-Rauch, Renate, Stroobants, Stijn, Andersson, Claes, Weigelt, Cecilia, Eistrup, Carl, Fogh, Jens, D'Hooge, Rudi, Gieselmann, VolkmarVolume:
17
Language:
english
Journal:
Molecular Therapy
DOI:
10.1038/mt.2008.305
Date:
April, 2009
File:
PDF, 1.68 MB
english, 2009