AAV2-mediated CLN2 gene transfer to rodent and non-human primate brain results in long-term TPP-I expression compatible with therapy for LINCL
Sondhi, D, Peterson, D A, Giannaris, E L, Sanders, C T, Mendez, B S, De, B, Rostkowski, A B, Blanchard, B, Bjugstad, K, Sladek, J R, Redmond, D E, Leopold, P L, Kaminsky, S M, Hackett, N R, Crystal, RVolume:
12
Language:
english
Journal:
Gene Therapy
DOI:
10.1038/sj.gt.3302549
Date:
November, 2005
File:
PDF, 676 KB
english, 2005