Helper-dependent adenoviral vectors for liver-directed gene therapy of primary hyperoxaluria type 1
Castello, R, Borzone, R, d’Aria, S, Annunziata, P, Piccolo, P, Brunetti-Pierri, NLanguage:
english
Journal:
Gene Therapy
DOI:
10.1038/gt.2015.107
Date:
November, 2015
File:
PDF, 3.65 MB
english, 2015