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A Single Intravenous rAAV Injection as Late as P20 Achieves Efficacious and Sustained CNS Gene Therapy in Canavan Mice
Ahmed, Seemin Seher, Li, Huapeng, Cao, Chunyan, Sikoglu, Elif M, Denninger, Andrew R, Su, Qin, Eaton, Samuel, Liso Navarro, Ana A, Xie, Jun, Szucs, Sylvia, Zhang, Hongwei, Moore, Constance, Kirschner,Volume:
21
Language:
english
Journal:
Molecular Therapy
DOI:
10.1038/mt.2013.138
Date:
December, 2013
File:
PDF, 1.13 MB
english, 2013