Treatment of retinitis pigmentosa due toMERTKmutations by ocular subretinal injection of adeno-associated virus gene vector: results of a phase I trial
Ghazi, Nicola G., Abboud, Emad B., Nowilaty, Sawsan R., Alkuraya, Hisham, Alhommadi, Abdulrahman, Cai, Huimin, Hou, Rui, Deng, Wen-Tao, Boye, Sanford L., Almaghamsi, Abdulrahman, Al Saikhan, Fahad, AlVolume:
135
Language:
english
Journal:
Human Genetics
DOI:
10.1007/s00439-016-1637-y
Date:
March, 2016
File:
PDF, 1.77 MB
english, 2016