Velaglucerase alfa enzyme replacement therapy in children and adolescents with type 3 Gaucher disease: Results of a 12-month multicenter, open-label phase 1/2 study
Tantawy, Azza A.G., El-Beshlawy, Amal, Marzouk, Iman, Bavdekar, Ashish, Qin, Yulin, Mellgard, Björn, Turkia, Hadhami BenVolume:
117
Language:
english
Journal:
Molecular Genetics and Metabolism
DOI:
10.1016/j.ymgme.2015.12.456
Date:
February, 2016
File:
PDF, 50 KB
english, 2016