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rAAV gene therapy in a Canavan’s disease mouse model reveals immune impairments and an extended pathology beyond the central nervous system.
Ahmed, Seemin Seher, Schattgen, Stefan A., Frakes, Ashley E., Sikoglu, Elif M., Su, Qin, Li, Jia, Hampton, Thomas G., Denninger, Andrew R., Kirschner, Daniel A., Kaspar, Brian, Matalon, Reuben, Gao, GLanguage:
english
Journal:
Molecular Therapy
DOI:
10.1038/mt.2016.68
Date:
April, 2016
File:
PDF, 2.05 MB
english, 2016