Intranasal gene delivery of AAV9 iduronidase: A non-invasive and effective gene therapy approach for prevention of neurologic disease in a murine model of mucopolysaccharidosis type I
Belur, Lalitha, Buckvold, Megan, Podetz-Pedersen, Kelly M., Riedl, Maureen, Vulchanova, Lucy, Hanson, Leah R., Fairbanks, Carolyn, Kozarsky, Karen, Frey, William H., Low, Walter C., Scott McIvor, R.Volume:
117
Language:
english
Journal:
Molecular Genetics and Metabolism
DOI:
10.1016/j.ymgme.2015.12.195
Date:
February, 2016
File:
PDF, 55 KB
english, 2016