Safe and Efficient Preclinical Gene Therapy for Pyruvate...

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Safe and Efficient Preclinical Gene Therapy for Pyruvate Kinase Deficiency

Garcia-Gomez, Maria, Calabria, Andrea, Garcia-Bravo, Maria, Benedicenti, Fabrizio, Kosinski, Penelope, López-Manzaneda, Sergio, Hill, Collin, Mañu-Pereira, María del Mar, Martín, Miguel A., Orman, Isr
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Language:
english
Journal:
Molecular Therapy
DOI:
10.1038/mt.2016.87
Date:
May, 2016
File:
PDF, 2.76 MB
english, 2016
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