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Limitations of drug registries to evaluate orphan medicinal products for the treatment of lysosomal storage disorders
Carla EM Hollak, Johannes MFG Aerts, Ségolène Aymé, Jeremy ManuelVolume:
6
Language:
english
DOI:
10.1186/1750-1172-6-16
Date:
December, 2011
File:
PDF, 270 KB
english, 2011