Histologic characterization of the progression of central nervous system pathology in the mucopolysaccharidosis IIIB (MPS IIIB, Sanfilippo syndrome type B) mouse model and bio-distribution and efficacy of the intracerebroventricular enzyme replacement therapy, BMN 250
Bagri, Anil, Harmon, Danielle, Vincelette, Jon, Vitelli, Catherine, Minto, Wesley, Yates, Bridget, Rigney, Sara, Santiago, Pam, Baridon, Brian, Xie, Lin, Gorostiza, Olivia, Christianson, Terri, Tiger,Volume:
117
Language:
english
Journal:
Molecular Genetics and Metabolism
DOI:
10.1016/j.ymgme.2015.12.187
Date:
February, 2016
File:
PDF, 69 KB
english, 2016