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Reveglucosidase alfa (BMN 701), a GILT-tagged recombinant human acid alpha glucosidase (rhGAA), evaluation in late-onset Pompe disease: Preliminary clinical efficacy and safety results of an extension study (72-week results)
Hiwot, T., Barohn, R., Bratkovic, D., Byrne, B., Desnuelle, C., Hughes, D., Laforêt, P., Mengel, E., Roberts, M., Yang, K., Heusner, C., Dummer, W.Volume:
25
Language:
english
Journal:
Neuromuscular Disorders
DOI:
10.1016/j.nmd.2015.06.453
Date:
October, 2015
File:
PDF, 222 KB
english, 2015