Phase I Open Label Liver-Directed Gene Therapy Clinical Trial for Acute Intermittent Porphyria
D’Avola, Delia, López-Franco, Esperanza, Sangro, Bruno, Pañeda, Astrid, Grossios, Nadina, Gil-Farina, Irene, Benito, Alberto, Twisk, Jaap, Paz, María, Ruiz, Juan, Schmidt, Manfred, Petry, Harald, HarpLanguage:
english
Journal:
Journal of Hepatology
DOI:
10.1016/j.jhep.2016.05.012
Date:
May, 2016
File:
PDF, 789 KB
english, 2016