Early treatment with laronidase improves clinical outcomes...

Orphanet Journal of Rare Diseases 2015 / 12 Vol. 10; Iss. 1

Early treatment with laronidase improves clinical outcomes in patients with attenuated MPS I: a retrospective case series analysis of nine sibships

Al-Sannaa, Nouriya A., Bay, Luisa, Barbouth, Deborah S., Benhayoun, Youssef, Goizet, Cyril, Guelbert, Norberto, Jones, Simon A., Kyosen, Sandra Obikawa, Martins, Ana Maria, Phornphutkul, Chanika, Reig
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Volume:
10
Language:
english
Journal:
Orphanet Journal of Rare Diseases
DOI:
10.1186/s13023-015-0344-4
Date:
December, 2015
File:
PDF, 1.33 MB
english, 2015
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