Allele-Selective Inhibition of Mutant Huntingtin with 2-Thio- and C5- Triazolylphenyl-Deoxythymidine-Modified Antisense Oligonucleotides
Østergaard, Michael E., Kumar, Pawan, Nichols, Josh, Watt, Andrew, Sharma, Pawan K., Nielsen, Poul, Seth, Punit P.Volume:
25
Language:
english
Journal:
Nucleic Acid Therapeutics
DOI:
10.1089/nat.2015.0547
Date:
October, 2015
File:
PDF, 1.07 MB
english, 2015