Long-term, high level hepatic secretion of acid α-glucosidase for Pompe disease achieved in non-human primates using helper-dependent adenovirus
Rastall, D P W, Seregin, S S, Aldhamen, Y A, Kaiser, L M, Mullins, C, Liou, A, Ing, F, Pereria-Hicks, C, Godbehere-Roosa, S, Palmer, D, Ng, P, Amalfitano, ALanguage:
english
Journal:
Gene Therapy
DOI:
10.1038/gt.2016.53
Date:
July, 2016
File:
PDF, 1.53 MB
english, 2016