A Potent Inhibitor of Protein Sequestration by Expanded Triplet (CUG) Repeats that Shows Phenotypic Improvements in a Drosophila Model of Myotonic Dystrophy
Luu, Long M., Nguyen, Lien, Peng, Shaohong, Lee, JuYeon, Lee, Hyang Yeon, Wong, Chun-Ho, Hergenrother, Paul J., Chan, H. Y. Edwin, Zimmerman, Steven C.Volume:
11
Language:
english
Journal:
ChemMedChem
DOI:
10.1002/cmdc.201600081
Date:
July, 2016
File:
PDF, 1.27 MB
english, 2016