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Impact of long-term elosulfase alfa treatment on respiratory function in patients with Morquio A syndrome
Hendriksz, Christian J., Berger, Kenneth I., Parini, Rossella, AlSayed, Moeenaldeen D., Raiman, Julian, Giugliani, Roberto, Mitchell, John J., Burton, Barbara K., Guelbert, Norberto, Stewart, Fiona, HVolume:
39
Language:
english
Journal:
Journal of Inherited Metabolic Disease
DOI:
10.1007/s10545-016-9973-6
Date:
November, 2016
File:
PDF, 510 KB
english, 2016