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Development of an optimized AAV2/5 gene therapy vector for Leber congenital amaurosis owing to defects in RPE65
Georgiadis, A, Duran, Y, Ribeiro, J, Abelleira-Hervas, L, Robbie, S J, Sünkel-Laing, B, Fourali, S, Gonzalez-Cordero, A, Cristante, E, Michaelides, M, Bainbridge, J W B, Smith, A J, Ali, R RLanguage:
english
Journal:
Gene Therapy
DOI:
10.1038/gt.2016.66
Date:
September, 2016
File:
PDF, 1.85 MB
english, 2016