Antisense Oligonucleotide-mediated Exon Skipping as a Systemic Therapeutic Approach for Recessive Dystrophic Epidermolysis Bullosa
Bremer, Jeroen, Bornert, Olivier, Nyström, Alexander, Gostynski, Antoni, Jonkman, Marcel F, Aartsma-Rus, Annemieke, van den Akker, Peter C, Pasmooij, Anna MGVolume:
5
Language:
english
Journal:
Molecular Therapy—Nucleic Acids
DOI:
10.1038/mtna.2016.87
Date:
October, 2016
File:
PDF, 2.26 MB
english, 2016