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In vivo correction of anaemia in β-thalassemic mice by γPNA-mediated gene editing with nanoparticle delivery
Bahal, Raman, Ali McNeer, Nicole, Quijano, Elias, Liu, Yanfeng, Sulkowski, Parker, Turchick, Audrey, Lu, Yi-Chien, Bhunia, Dinesh C., Manna, Arunava, Greiner, Dale L., Brehm, Michael A., Cheng, ChristVolume:
7
Language:
english
Journal:
Nature Communications
DOI:
10.1038/ncomms13304
Date:
October, 2016
File:
PDF, 1.32 MB
english, 2016