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Capturing the biology of disease severity in a PSC-based model of familial dysautonomia
Zeltner, Nadja, Fattahi, Faranak, Dubois, Nicole C, Saurat, Nathalie, Lafaille, Fabien, Shang, Lei, Zimmer, Bastian, Tchieu, Jason, Soliman, Mohamed A, Lee, Gabsang, Casanova, Jean-Laurent, Studer, LoLanguage:
english
Journal:
Nature Medicine
DOI:
10.1038/nm.4220
Date:
November, 2016
File:
PDF, 2.50 MB
english, 2016