Ocular and systemic safety of a recombinant AAV8 vector for X-linked retinoschisis gene therapy: GLP studies in rabbits and Rs1-KO mice
Marangoni, Dario, Bush, Ronald A, Zeng, Yong, Wei, Lisa L, Ziccardi, Lucia, Vijayasarathy, Camasamudram, Bartoe, Joshua T, Palyada, Kiran, Santos, Maria, Hiriyanna, Suja, Wu, Zhijian, Colosi, Peter, SVolume:
3
Year:
2016
Language:
english
Journal:
Molecular Therapy - Methods & Clinical Development
DOI:
10.1038/mtm.2016.11
File:
PDF, 2.41 MB
english, 2016