124. Therapeutic Correction of an LCA-Causing Splice Defect...

Molecular Therapy 2016 / 05 Vol. 24

124. Therapeutic Correction of an LCA-Causing Splice Defect in the CEP290 Gene by CRISPR/Cas-Mediated Gene Editing

Maeder, Morgan L., Mepani, Rina, Gloskowski, Sebastian, Skor, Maxwell, Collins, McKensie, Shen, Shen, Gotta, Gregory, Marco, Eugenio, Barrera, Luis, Jayaram, Hari, Bumcrot, David
How much do you like this book?
What’s the quality of the file?
Download the book for quality assessment
What’s the quality of the downloaded files?
Volume:
24
Language:
english
Journal:
Molecular Therapy
DOI:
10.1016/s1525-0016(16)32933-1
Date:
May, 2016
File:
PDF, 312 KB
english, 2016
Conversion to is in progress
Conversion to is failed