373. Optimization of AAV-Gene Therapy for GM1-Gangliosidosis
Stoica, Lorelei, Todeasa, Sophia, Lata, Jaclyn, Martin, Douglas, Sena-Esteves, MiguelVolume:
24
Language:
english
Journal:
Molecular Therapy
DOI:
10.1016/s1525-0016(16)33182-3
Date:
May, 2016
File:
PDF, 268 KB
english, 2016