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500. Gene Therapy Rescues Disease Phenotype in the Oculopharyngeal Muscular Dystrophy Mouse Model
Dickson, George, Malerba, Alberto, Klein, Pierre, Jarmin, Susan, Bachtarzi, Houria, Ferry, Arnaud, Butler-Browne, Gillian, Suhy, David, Graham, Michael, Trollet, CapucineVolume:
24
Language:
english
Journal:
Molecular Therapy
DOI:
10.1016/s1525-0016(16)33309-3
Date:
May, 2016
File:
PDF, 351 KB
english, 2016